Gene therapy clinical trials for rare Angelman syndrome put on hold
Surupa Chakraborty, Amity University Kolkata A new gene therapy clinical trial for treating Angelman syndrome has been put to hold after two candidates temporarily lost their ability to walk. GTX102, the drug used in the clinical trial was developed by a California-based biopharmaceutical company Ultragenyx, in collaboration with GeneTx, a Florida-based biotech startup. The trial […]